Europe to see first genetically engineered patients using gene-splicing therapy


Europe will see its first genetically engineered patients using a groundbreaking gene-splicing therapy this year after regulators approved trials.

The biotech company Crispr Therapeutics is hoping to cure the disease beta thalassaemia, a devastating blood disorder which reduces the production of haemoglobin, the protein which carries oxygen to cells.

Without sufficient oxygen, sufferers can be left with bone deformities, severe anaemia, slow growth, fatigue and shortness of breath.

The disease is caused by a genetic mutation in the HBB gene, but scientists are confident that they can alter the body’s code to fix the problem and restore healthy levels of haemoglobin.

It will be the first human…



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